Atlanta, GA August 6, 2019 – Emil Kakkis, MD, PhD, joins the Board of Directors for Odylia Therapeutics. Kakkis is the CEO, President and Founder of Ultragenyx Pharmaceutical Inc., which is committed to developing and commercializing treatments for multiple rare and ultra-rare diseases. He brings to Odylia vast knowledge...
SOUTH PLAINFIELD, N.J., and BOSTON, M.A. - July 1, 2019 – PTC Therapeutics, Inc. (NASDAQ: PTCT) and Odylia Therapeutics today announced a strategic collaboration to develop novel gene therapies in rare inherited retinal diseases (IRDs) utilizing the Anc80 vector system developed by researchers at Massachusetts...
Lara Aronoff Dorfman joins Odylia Therapeutics as the Director of Business Development. Her focus for this unique nonprofit biotech company will be raising capital through philanthropy, primarily from foundations and corporate giving. Increased funds will allow Odylia to have a greater impact on shifting the...
Scott Dorfman, Odylia Therapeutics CEO, was recently a featured guest on Partners4Access Weekly Podcast. A recording of the podcast entitled “Rare Disease, Cell and Gene Therapy Weekly Roundup” can be found here. Produced by Partners4Access, global experts in access for orphan drug, cell and gene...
Odylia CSO Harrison Brown, PhD spoke at the 2019 meeting of the American Society of Gene and Cell Therapy on the issues restricting the development and clinical application of gene therapies for rare genetic diseases. He discussed the specific challenges facing ultra-rare indications, especially those...
March 26, 2019 (Boston, MA) Odylia Therapeutics Chief Scientific Officer Harrison Brown led a workshop on the challenges and solutions to the development of AAV gene therapies for rare disorders. Held at the 3rd Annual Gene Therapy For Rare Disorders Conference in Boston, MA, this...
March 25, 2019 (Boston, MA) The inaugural meeting of the Odylia Gene Therapy Pre-Competitive Consortium has been held at the Massachusetts Eye and Ear campus in Boston, MA. This meeting brought together a select group of thought leaders in the gene therapy field...
Researcher and entrepreneur Luk Vandenberghe thinks he can transport genes into cells much more efficiently by improving the viral vectors that carry them. He also describes how Odylia can leverage these new technologies to bring therapies for ultra-rare disorders into the clinic. Read the full Nature...
Odylia CSO Harrison Brown speaks to the Charles River World Congress on the promises and challenges of gene therapy for rare diseases. Video link: Delivering the DNA...
Odylia CEO Scott Dorfman presented the Odylia concept to the National Institutes of Health and National Center for Advancing Translational Sciences (NCATS) at a conference on The Growing Promise of Gene Therapy Approaches. Please skip to 4:18:00 to see the Odylia talk and followup panel discussion. Please click...